FDA Approves First Treatment for Patients with Rare Inherited Blood Clotting Disorder

FDA Approves First Treatment for Patients with Rare Inherited Blood Clotting Disorder

Upworthy

Published

Today, the U.S. Food and Drug Administration approved Adzynma, the first recombinant (genetically engineered) protein product indicated for prophylactic (preventive) or on demand enzyme replacement therapy (ERT) in adult and pediatric patients with congenital thrombotic thrombocytopenic purpura…

#adzynma #ert #fda #petermarks #phd #cttp #adamts13 #adyznma #ttp #reviewvoucher

Full Article